RARECast

548 Avsnitt

1. Accelerating the Development of Genetic Medicines with AI

   Publicerades: 2023-12-07
2. Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

   Publicerades: 2023-11-30
3. In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

   Publicerades: 2023-11-22
4. In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

   Publicerades: 2023-11-16
5. Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

   Publicerades: 2023-11-09
6. A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

   Publicerades: 2023-11-02
7. Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

   Publicerades: 2023-10-26
8. Turning Grief into Action

   Publicerades: 2023-10-19
9. A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

   Publicerades: 2023-10-12
10. How the Woolly Mammoth Beat a Path to Better Gene Therapies

    Publicerades: 2023-10-05
11. A Genetic Counselor’s Journey into Patient Advocacy

    Publicerades: 2023-09-28
12. A Company in the Fold of Rare Disease

    Publicerades: 2023-09-21
13. Disabling Antibodies that Drive Rare, Immunological Conditions

    Publicerades: 2023-09-14
14. Keeping the Sentinels of the Brain Vigilant

    Publicerades: 2023-09-07
15. Considering the Unfinished Work in Cystic Fibrosis

    Publicerades: 2023-08-31
16. How to Advocate for Yourself as You Battle Cancer

    Publicerades: 2023-08-24
17. Targeting Neuroinflammation to Treat ALS

    Publicerades: 2023-08-17
18. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

    Publicerades: 2023-08-10
19. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

    Publicerades: 2023-08-03
20. Inhibiting Electrical Activity in Rare, Seizure Disorders

    Publicerades: 2023-07-27