RARECast

548 Avsnitt

1. Addressing a Shortage of Genetic Counselors with AI

   Publicerades: 2024-04-25
2. A Small Molecule Therapy to Regenerate Muscle in People with DMD

   Publicerades: 2024-04-18
3. Forging a Faster Path for Gene Therapies

   Publicerades: 2024-04-11
4. Determining the Value of Rare Disease Therapies

   Publicerades: 2024-04-04
5. Buying and Building a Gene Therapy Presence

   Publicerades: 2024-03-28
6. A Clinical Trial Failure Derails a Promising Technology

   Publicerades: 2024-03-21
7. Helping People with Undiagnosed Rare Diseases Find Answers

   Publicerades: 2024-03-14
8. Speeding and Scaling the Development of Genome Editing Therapies

   Publicerades: 2024-03-07
9. Getting a Next-Generation Genome Editing Therapy for Sickle Cell Disease Back on Track

   Publicerades: 2024-02-29
10. Trying to Break a Leg in a Wheelchair

    Publicerades: 2024-02-22
11. A Drug Developer that Makes Pediatric Cancers a Priority

    Publicerades: 2024-02-15
12. Harnessing the Body’s Natural RNA Machinery to Treat Diseases

    Publicerades: 2024-02-08
13. Targeting the Leading Cause of Death in Friedreich’s Ataxia with a Gene Therapy

    Publicerades: 2024-02-01
14. How Inhaled mRNA May Help Rare Disease Patients Breathe Easier

    Publicerades: 2024-01-25
15. Changing What’s Possible with Cell and Gene Therapies

    Publicerades: 2024-01-18
16. Why Flying with a Wheelchair Is a Civil Rights Issue

    Publicerades: 2024-01-11
17. Mapping Spheres of Influence

    Publicerades: 2024-01-04
18. Bringing Precision to the Treatment of Rare Cancers

    Publicerades: 2023-12-28
19. The Challenges of Developing a Therapy for Pregnant Women with A Rare Condition

    Publicerades: 2023-12-21
20. How One Drug Developer Is Addressing Health Inequities

    Publicerades: 2023-12-14